ABSTRACT

IJSR

International Journal of Scientific Research

2277 - 8179

Indian Society for Health and Advanced Research

ijsr-7-6-15756

Original Research Paper

THE MOST EXCITING INNOVATION IN GENE THERAPY

Rao

M.V

Dr. Sripada

Pallavi.T

Dr. Ramanaiah.C.J

Dr. Sateesh.Babu.A

Dr.

June 2018

7 6 01 02 ABSTRACT

Gene therapy is viable, available and reliable. Gene therapy or human gene transfer is the process of replacing defective genes in a cell with healthy

genes. The defective genes produce genetic diseases. People with genetic disorders such as Alzheimer’s disease, Huntington’s’ disease and

Parkinson’s disease are among those who require gene therapy. The key objective a modern gene therapy involves. Replacing defective (mutated)

gene/s that causes disease with a healthy copy of the gene/s. Introducing a new functional copy of gene/s into the cells to help fight a disease .

Inactivating, or “knocking out,” (silencing; gene silencing) a mutated gene that is functioning improperly. In the present scenario gene therapy is

not only limited to therapeutic delivery of gene/s but also regulation of gene functioning as well.